Expansion has assembled a focused pipeline of compositions targeting expansion repeat disorders, a set of approximately 30 genetic diseases for which there are no satisfactory treatments.
Discovery
Preclinical
Phase 1
DM1
Myotonic Dystrophy Type 1
DM2
Myotonic Dystrophy Type 2
Undisclosed
Expansion Repeat Disorder
Undisclosed
Non-Expansion Repeat Disorder