Pipeline of Compositions

Expansion has assembled a focused pipeline of compositions targeting expansion repeat disorders, a set of approximately 30 genetic diseases for which there are no satisfactory treatments.

Discovery

Preclinical

Phase 1

DM1

Myotonic Dystrophy Type 1

Lead Selection

30%

DM2

Myotonic Dystrophy Type 2

Discovery

20%

Undisclosed

Expansion Repeat Disorder

Discovery

20%

Undisclosed

Non-Expansion Repeat Disorder

Discovery

15%